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Revised Hammersmith Scale for Spinal Muscular Atrophy: A SMA specific clinical outcome assessment tool

  • Danielle Ramsey
  • , Mariacristina Scoto
  • , Anna Mayhew
  • , Marion Main
  • , Elena S Mazzone
  • , Jacqueline Montes
  • , Roberto de Sanctis
  • , Sally Dunaway Young
  • , Rachel Salazar
  • , Allan M Glanzman
  • , Amy Pasternak
  • , Janet Quigley
  • , Elizabeth Mirek
  • , Tina Duong
  • , Richard Gee
  • , Matthew Civitello
  • , Gihan Tennekoon
  • , Marika Pane
  • , Maria Carmela Pera
  • , Kate Bushby
  • John Day, Basil T Darras, Darryl De Vivo, Richard Finkel, Eugenio Mercuri, Francesco Muntoni

    Research output: Contribution to journalArticlepeer-review

    98 Citations (Scopus)
    77 Downloads (Pure)

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