Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

Julia Alter, Fang Lou, Adam Rabinowitz, HaiFang Yin, Jeffrey Rosenfeld, Steve D Wilton, Terence A Partridge, Qi Long Lu

Research output: Contribution to journalArticlepeer-review

408 Citations (Scopus)

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Keyphrases

Biochemistry, Genetics and Molecular Biology

Medicine and Dentistry

Neuroscience